Gene therapy

FDA approves $2M medicine, most expensive ever

FDA approves $2M medicine, most expensive ever

Business 05/24/19, 13:36

U.S. regulators have approved the most expensive medicine ever, for a disorder that destroys a baby's muscle control and kills nearly all of those with the most common variant of the disease within a couple years.The treatment is priced at $2.125 million. Out-of-pocket costs for patients will vary based on ...

Doctors use HIV in gene therapy to fix ‘bubble boy’ disease

Doctors use HIV in gene therapy to fix ‘bubble boy’ disease

U.S. 04/17/19, 16:06

They were born without a working germ-fighting system, every infection a threat to their lives. Now eight babies with "bubble boy disease" have had it fixed by a gene therapy made from one of the immune system's worst enemies — HIV, the virus that causes AIDS.A study out Wednesday details ...

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